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Development code · Biologic

ION363

ION363 is a development code for Ulefnersen (ION363), developed by Ionis Pharmaceuticals, Inc..

Status
Phase 3 for Amyotrophic lateral sclerosis
Mechanism
FUS Inhibitor
Developer
Ionis Pharmaceuticals, Inc.

Programs

  • Ulefnersen (ION363) for Amyotrophic lateral sclerosisPhase 3Active

Also known as

  • ION-363
  • Jacifusen
  • Ulefnersen
  • 2589926-25-3

View the full Ulefnersen (ION363) profile →

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