Development code · Biologic
ION-363
ION-363 is a development code for Ulefnersen (ION363), developed by Ionis Pharmaceuticals, Inc..
- Status
- Phase 3 for Amyotrophic lateral sclerosis
- Mechanism
- FUS Inhibitor
- Developer
- Ionis Pharmaceuticals, Inc.
Programs
Also known as
- ION363
- Jacifusen
- Ulefnersen
- 2589926-25-3